Patient and caregiver spinal muscular atrophy treatment attribute preferences in Latin America.
Saenz V. et al, (2025), J Neuromuscul Dis
A systematic review on motor outcome measures in congenital myopathy.
Woods M. et al, (2025), Neuromuscul Disord
Pain management in preterm infants with necrotizing enterocolitis: an international expert consensus statement
ten Barge JA. et al, (2025), European Journal of Pediatrics, 184
A real-world analysis of the impact of X-linked myotubular myopathy on caregivers in the United States.
Duong T. et al, (2025), Orphanet J Rare Dis, 20
Data-driven consideration of genetic disorders for global genomic newborn screening programs.
Minten T. et al, (2025), Genet Med, 27
The TyphiNET data visualisation dashboard: unlocking Salmonella Typhi genomics data to support public health.
Dyson ZA. et al, (2025), Genome Med, 17
A phase 1/2a clinical trial to assess safety and immunogenicity of an adenoviral-vectored capsular group B meningococcal vaccine
Dold C. et al, (2025), Science Translational Medicine, 17
Genome-wide association meta-analysis of age at onset of walking in over 70,000 infants of European ancestry.
Gui A. et al, (2025), Nat Hum Behav
Immune-epithelial-stromal networks define the cellular ecosystem of the small intestine in celiac disease.
FitzPatrick MEB. et al, (2025), Nat Immunol
Gene therapy approval for Duchenne muscular dystrophy: a European perspective.
Jolly H. et al, (2025), Lancet, 405, 1572 - 1573
Consultation report - considerations for a regulatory pathway for bivalent Salmonella Typhi/Paratyphi A vaccines for use in endemic countries.
Ibarz-Pavon AB. et al, (2025), Vaccine, 56
Distinct type I and II interferon responses direct cortical and medullary thymic epithelial cell development.
Mohammed A. et al, (2025), Sci Immunol, 10
Effectiveness of biomarker-guided duration of antibiotic treatment in children hospitalised with confirmed or suspected bacterial infection: the BATCH RCT.
Waldron C-A. et al, (2025), Health Technol Assess, 29, 1 - 125
Severe Parvovirus B19-Associated Myocarditis in Children in the Post-COVID-19 Era: A Multicenter Observational Cohort Study.
Russell N. et al, (2025), Open Forum Infect Dis, 12
Engineering of extracellular vesicles for efficient intracellular delivery of multimodal therapeutics including genome editors.
Liang X. et al, (2025), Nat Commun, 16
CMV serostatus is associated with improved survival and delayed toxicity onset following anti-PD-1 checkpoint blockade
Milotay G. et al, (2025), Nature Medicine
The aetiologies, mortality, and disability of non-traumatic coma in African children: a systematic review and meta-analysis.
Ray STJ. et al, (2025), Lancet Glob Health
Author Correction: Immunogenic recombinant Mayaro virus-like particles present natively assembled glycoprotein.
Kim YC. et al, (2025), NPJ Vaccines, 10
Influence of context on engagement with COVID-19 testing: a scoping review of barriers and facilitators to testing for healthcare workers, care homes and schools in the UK.
Andersen-Waine B. et al, (2025), BMJ Open, 15