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Publications

Long-term dystrophin restoration supports development of splice correction therapy for DMD patients with exon 2 duplications

Roberts TC., (2023), Molecular Therapy Methods and Clinical Development, 31

EV-mediated promotion of myogenic differentiation is dependent on dose, collection medium, and isolation method

Hanson B. et al, (2023), Molecular Therapy - Nucleic Acids, 33, 511 - 528

Therapeutic approaches for Duchenne muscular dystrophy.

Roberts TC. et al, (2023), Nat Rev Drug Discov

An extracellular vesicle delivery platform based on the PTTG1IP protein

Perez CM. et al, (2023)

Investigating Eukaryotic Elongation Factor 2 Kinase/Eukaryotic Translation Elongation Factor 2 Pathway Regulation and Its Role in Protein Synthesis Impairment during Disuse-Induced Skeletal Muscle Atrophy.

Vilchinskaya N. et al, (2023), Am J Pathol, 193, 813 - 828

Multimodal engineering of extracellular vesicles for efficient intracellular protein delivery

Liang X. et al, (2023)

Non-uniform dystrophin re-expression after CRISPR-mediated exon excision in the dystrophin/utrophin double-knockout mouse model of DMD.

Hanson B. et al, (2022), Mol Ther Nucleic Acids, 30, 379 - 397

Exon skipping induces uniform dystrophin rescue with dose-dependent restoration of serum miRNA biomarkers and muscle biophysical properties.

Chwalenia K. et al, (2022), Mol Ther Nucleic Acids, 29, 955 - 968

Extracellular vesicle-mediated promotion of myogenic differentiation is dependent on dose, collection media composition, and isolation method

Hanson B. et al, (2022)

AR cooperates with SMAD4 to maintain skeletal muscle homeostasis.

Forouhan M. et al, (2022), Acta Neuropathol, 143, 713 - 731

AR cooperates with SMAD4 to maintain skeletal muscle homeostasis

Rinaldi C. et al, (2022)

Nuclear microRNA-466c regulates Vegfa expression in response to hypoxia

Laitinen P. et al, (2022), PLoS ONE, 17

Non-uniform dystrophin re-expression after CRISPR-mediated exon excision in the dystrophin/utrophin double-knockout mouse model of DMD

Hanson B. et al, (2022)

PPMO-mediated exon skipping induces uniform sarcolemmal dystrophin rescue with dose-dependent restoration of circulating microRNA biomarkers and muscle biophysical properties

Chwalenia K. et al, (2022)

Enhancing the Therapeutic Potential of Extracellular Vesicles Using Peptide Technology

Martin Perez C. et al, (2022), Methods in Molecular Biology, 2383, 119 - 141

Author Correction: GAPDH controls extracellular vesicle biogenesis and enhances the therapeutic potential of EV mediated siRNA delivery to the brain.

Dar GH. et al, (2021), Nat Commun, 12

GAPDH controls extracellular vesicle biogenesis and enhances the therapeutic potential of EV mediated siRNA delivery to the brain.

Dar GH. et al, (2021), Nat Commun, 12

Amelioration of systemic inflammation via the display of two different decoy protein receptors on extracellular vesicles.

Gupta D. et al, (2021), Nat Biomed Eng, 5, 1084 - 1098

Gene therapy with AR isoform 2 rescues spinal and bulbar muscular atrophy phenotype by modulating AR transcriptional activity.

Lim WF. et al, (2021), Sci Adv, 7

Molecular correction of Duchenne muscular dystrophy by splice modulation and gene editing.

Hanson B. et al, (2021), RNA Biol, 1 - 15

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