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Recent publications

Uniform sarcolemmal dystrophin expression is required to prevent extracellular microRNA release and improve dystrophic pathology.

van Westering TLE. et al, (2019), J Cachexia Sarcopenia Muscle

Doublecortin like kinase 1 regulates α-Synuclein levels and toxicity.

Vázquez-Vélez GE. et al, (2019), J Neurosci

Wrangling RNA: Antisense oligonucleotides for neurological disorders

Talbot K. and Wood MJA., (2019), Science Translational Medicine, 11, eaay2069 - eaay2069

Peptide-conjugated oligonucleotides evoke long-lasting myotonic dystrophy correction in patient-derived cells and mice.

Klein AF. et al, (2019), J Clin Invest

Peptide-conjugate antisense based splice-correction for Duchenne muscular dystrophy and other neuromuscular diseases.

Tsoumpra MK. et al, (2019), EBioMedicine, 45, 630 - 645

The viral protein corona directs viral pathogenesis and amyloid aggregation.

Ezzat K. et al, (2019), Nat Commun, 10

Extracellular microRNAs exhibit sequence-dependent stability and cellular release kinetics.

Coenen-Stass AML. et al, (2019), RNA Biol, 16, 696 - 706

Extracellular vesicle-based therapeutics: natural versus engineered targeting and trafficking.

Murphy DE. et al, (2019), Exp Mol Med, 51

Exosome-Mediated miR-29 Transfer Reduces Muscle Atrophy and Kidney Fibrosis in Mice.

Wang H. et al, (2019), Mol Ther, 27, 571 - 583

The potential of utrophin and dystrophin combination therapies for Duchenne muscular dystrophy.

Guiraud S. et al, (2019), Hum Mol Genet

Cmah-dystrophin deficient mdx mice display an accelerated cardiac phenotype that is improved following peptide-PMO exon skipping treatment.

Betts CA. et al, (2019), Hum Mol Genet, 28, 396 - 406

Embryonic myosin is a regeneration marker to monitor utrophin-based therapies for DMD.

Guiraud S. et al, (2019), Hum Mol Genet, 28, 307 - 319

Considerations and Implications in the Purification of Extracellular Vesicles - A Cautionary Tale.

Lee YXF. et al, (2019), Front Neurosci, 13

Evaluation of Cell-Penetrating Peptide Delivery of Antisense Oligonucleotides for Therapeutic Efficacy in Spinal Muscular Atrophy.

Hammond SM. et al, (2019), Methods Mol Biol, 2036, 221 - 236

Comprehensive RNA-Sequencing Analysis in Serum and Muscle Reveals Novel Small RNA Signatures with Biomarker Potential for DMD.

Coenen-Stass AML. et al, (2018), Mol Ther Nucleic Acids, 13, 1 - 15

UFLC-Derived CSF Extracellular Vesicle Origin and Proteome.

Thompson AG. et al, (2018), Proteomics, 18

A fusion peptide directs enhanced systemic dystrophin exon skipping and functional restoration in dystrophin-deficient mdx mice.

Yin H. et al, (2018), Hum Mol Genet

Cell-Penetrating Peptide Conjugates of Steric Blocking Oligonucleotides as Therapeutics for Neuromuscular Diseases from a Historical Perspective to Current Prospects of Treatment.

Gait MJ. et al, (2018), Nucleic Acid Ther

Light modulation ameliorates expression of circadian genes and disease progression in spinal muscular atrophy mice.

Walter LM. et al, (2018), Hum Mol Genet, 27, 3582 - 3597

PPMO's as Therapeutic Modulators for Myotonic Dystrophy Type 1

Holland A. et al, (2018), JOURNAL OF PEPTIDE SCIENCE, 24, S169 - S170

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