Cookies on this website
We use cookies to ensure that we give you the best experience on our website. If you click 'Continue' we'll assume that you are happy to receive all cookies and you won't see this message again. Click 'Find out more' for information on how to change your cookie settings.

Gene therapies for polyglutamine diseases

Chapter

Matos C. et al, (2020), Polyglutamine Disorders

Extracellular microRNAs exhibit sequence-dependent stability and cellular release kinetics.

Journal article

Coenen-Stass AML. et al, (2019), RNA Biol, 16, 696 - 706

Safety profile of the intravenous administration of brain-targeted stable nucleic acid lipid particles

Journal article

Conceição M. et al, (2016), Data in Brief, 6, 700 - 705

Overexpression of Mutant Ataxin-3 in Mouse Cerebellum Induces Ataxia and Cerebellar Neuropathology

Journal article

Nóbrega C. et al, (2013), The Cerebellum, 12, 441 - 455