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Crossing the finish line towards a disease-modifying treatment for Angelman syndrome.

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Judson MC. et al, (2026), J Neurodev Disord, 18

Enhanced muscle uptake of chemically optimized miR-23b antisense oligonucleotides as lead compounds for myotonic dystrophy type 1.

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González-Martínez I. et al, (2026), Am J Hum Genet, 113, 529 - 547

Targeted BDNF upregulation via upstream open reading frame disruption.

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Feng N. et al, (2026), Mol Ther, 34, 1652 - 1671

Advances in Alphavirus and Flavivirus Research II.

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Kim YC. and Reyes-Sandoval A., (2026), Viruses, 18

Structure-guided design of a PfCyRPA-based vaccine against blood-stage malaria.

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Alam N. et al, (2026), EMBO Mol Med, 18, 873 - 890

Structure-guided design of a PfCyRPA-based vaccine against blood-stage malaria.

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Alam N. et al, (2026), EMBO Mol Med, 18, 873 - 890

Broad lessons from negative trials in rare diseases.

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Servais L. and Oskoui M., (2026), Lancet Neurol, 25, 215 - 217

Advancing treatment of spinal muscular atrophy through inhibition of the myostatin signaling pathway.

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Finkel RS. et al, (2026), Expert Rev Neurother, 26, 211 - 225

Pneumococcal colonisation and mucosal immunity in adults with asthma following experimental human challenge

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Reiné J. et al, (2026), BMJ Immunology, 1, e000012 - e000012

Securing the future of immunisation: ESCMID’s vision

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Ramasamy MN. et al, (2026), CMI Communications, 3, 105167 - 105167

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