A fusion peptide directs enhanced systemic dystrophin exon skipping and functional restoration in dystrophin-deficient mdx mice.

Yin H., Moulton HM., Betts C., Seow Y., Boutilier J., Iverson PL., Wood MJA.

DOI

10.1093/hmg/ddy377

Type

Journal

Hum Mol Genet

Publication Date

15/02/2019

Volume

28

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