Preclinical studies of WVE-210201, an investigational stereopure antisense oligonucleotide in development for the treatment of patients with duchenne muscular dystrophy (DMD)
Panzara M., Zhang J., Rinaldi C., McClorey G., Bowman K., Butler D., Dodart J., Frank-Kamenetsky M., Iwamoto N., Kothari N., Lu G., Mathieu S., M M., Melkonian M., Menon S., Standley S., Yang H., Zhong Z., Wood M., Vargeese C.