Delivery of oligonucleotides to bone marrow to modulate ferrochelatase splicing in a mouse model of Erythropoietic Protoporphyria

Halloy F., Iyer PS., Ćwiek P., Ghidini A., Barman-Aksözen J., van Wijk NW-V., Theocharides A., Minder EI., Schneider-Yin X., Schümperli D., Hall J.

DOI

10.1101/2020.02.14.949297

Type

Preprint

Publication Date

16/02/2020

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