Enhanced muscle uptake of chemically optimized miR-23b antisense oligonucleotides as lead compounds for Myotonic Dystrophy type 1

González-Martínez I., Cerro-Herreros E., Carrascosa-Sàez M., García-Rey A., Piqueras-Losilla D., Colom-Rodrigo A., Moreno N., Chakraborty M., Huguet-Lachon A., González-Barriga A., Naldaiz-Gastesi N., Dehesa M., Barquero N., Varela MA., López de Munain A., Eritja R., Gourdon G., López-Castel A., Pérez-Alonso M., Llamusi B., Artero R.

DOI

10.1101/2025.07.30.667638

Type

Preprint

Publication Date

2026-02-02T00:00:00+00:00

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